Booster toward new scientific breaktroughs in rare and pediatric diseases
ABOUT THE MOONSHOT
95% of the 6,000-7,000 identified rare diseases don’t have an approved therapy. For most of these diseases, research is effectively non-existent. The search for new treatments is thwarted by enormous scientific challenges. At the current pace, it would take over 100 years to develop treatments for all rare conditions.
Public-private partnerships could help pool resources to solve problems more quickly, reduce fragmentation and scale up existing initiatives to make a real difference for patients. That’s why a coalition of partners is joining forces to accelerate research in rare and paediatric diseases and bring new therapies to patients.
Latest news
18 Nov 2024
Breaking barriers in Rare Disease Research: The Rare Disease Moonshot at two years
Rare diseases, despite affecting millions worldwide, remain an underserved area in medical research. Over 7,000 rare diseases have been identified, yet fewer than 5% have available treatments. This si...
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18 Oct 2024
Virtual Event – Innovating for Impact: Shaping the Future of Rare Disease Treatment
Millions of Europeans are living with rare diseases where no treatment option exists.
How can the work from the public and private sector help in accelerating research and raise awaren...
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16 Apr 2024
Translational research needs recommendations
The Rare Diseases (RD) Moonshot was set up to boost public private collaborations in the areas where there are with no treatment options and there is no R&D going on.
The RD Moonshot part...
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