Booster toward new scientific breaktroughs in rare and pediatric diseases
ABOUT THE MOONSHOT
95% of the 6,000-7,000 identified rare diseases don’t have an approved therapy. For most of these diseases, research is effectively non-existent. The search for new treatments is thwarted by enormous scientific challenges. At the current pace, it would take over 100 years to develop treatments for all rare conditions.
Public-private partnerships could help pool resources to solve problems more quickly, reduce fragmentation and scale up existing initiatives to make a real difference for patients. That’s why a coalition of partners is joining forces to accelerate research in rare and paediatric diseases and bring new therapies to patients.
Latest news
14 May 2025
Rare Disease Moonshot’s contribution to the Consultation on the next Multiannual Financial Framework
Introduction
The Rare Disease Moonshot is a multi-stakeholder initiative uniting public and private actors, researchers, clinicians, patients, and funders to advance research and care for the 30 mill...
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18 Apr 2025
Rare Disease Moonshot’s contribution to the Call for Evidence on the EU Life Science Strategy
Our submission on the call for evidence on the new Strategy for European Life Sciences can be found here.
The Rare Disease Moonshot welcomes the European Life Sciences Strategy (LSS) as a transf...
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14 Mar 2025
Rare Disease Moonshot contribution to the Call for Evidence on the EU Start-up and Scale-up Strategy
Start-ups and scale-ups play a crucial role in the development of innovative medicines in high unmet needs areas, such as rare disease, paediatric medicines or personalized medicines. To overcome regu...
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